Attacking a rare disease at its source with gene therapy
Treating the rare disease MPS I is a challenge. MPS I, caused by the deficiency of a key enzyme called IDUA, eventually leads to the abnormal accumulation of certain molecules and cell death.
Stem Cell Research
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In some genetic cases of microcephaly, stem cells fail to launch
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Embryonic gene Nanog reverses aging in adult stem cells
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Gene controls regeneration of injured muscle by adult stem cells
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Breakthrough in scaling up life-changing stem cell production
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New procedure allows long-term culturing of adult stem cells
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Stem cell transplant from young to old can heal stomach ulcers
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Scientists discover oldest plant root stem cells
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Penn bioengineers show why lab-made stem cells might fail: Errors in DNA folding
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Stem cell therapy improves outcomes in severe heart failure
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A quartet of genes controls growth of blood stem cells
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New way to harvest stem cells better for donors
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Oncogene controls stem cells in early embryonic development
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Hacking the programs of cancer stem cells
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Combining adult stem cells with hormone may speed bone fracture healing
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Discovery of an embryonic switch for cancer stem cell generation